Primary Recipient

SCRIPPS RESEARCH INSTITUTE, THE

Amount

$772,062.00

Award Date

9/01/2010

Administering Agency

Health and Human Services, Department of / National Institutes of Health

CDFA Number

93.701

CDFA Program Title

Trans-NIH Recovery Act Research Support

Description

The overall purpose is to study the cellular efficacy of designed small molecules targerting the RNA that causes myotonic dystrophy type 1 (DM1). Compounds will be optimized by competing in vitro assays to determine potency and in vivo assays to determin